Wiskott-Aldrich syndrome: Long-term results of gene therapy developed
A single infusion of genetically corrected autologous hematopoietic stem cells can provide lasting clinical benefits for patients with Wiskott-Aldrich syndrome, a rare genetic disorder that impairs immune and platelet function, exposing affected children from an early age to severe infections, bleed
<p>A single infusion of genetically corrected autologous hematopoietic stem cells can provide lasting clinical benefits for patients with Wiskott-Aldrich syndrome, a rare genetic disorder that impairs immune and platelet function, exposing affected children from an early age to severe infections, bleed</p>